UNIVERSITY OF CALIFORNIA BERKELEY
Research Project I: AAV-CRISPR to Treat Huntington's Disease
Research Project I: AAV-CRISPR to Treat Huntington's Disease is a funding opportunity from UNIVERSITY OF CALIFORNIA BERKELEY, up to 427885, closing April 30, 2028.
Apr 30, 2028
(639d left)Overview
PROJECT SUMMARY / ABSTRACT Background: Huntington's disease (HD) is a fatal, dominant neurogenetic disorder caused by polyglutamine repeat expansion in exon 1 of the HD gene encoding huntingtin (HTT). It is estimated that 1−3 in every 10,000 persons (nearly 30,000 in the USA) have HD. Patients suffer from…